Table of Content

1. Executive Summary
   1. Global Lysosomal Storage Disease Therapeutics Market Snapshot, 2025 and 2032
   2. Market Opportunity Assessment, 2025 - 2032, US$ Bn
   3. Key Market Trends
   4. Future Market Projections
   5. Premium Market Insights
   6. Industry Developments and Key Market Events
   7. PMR Analysis and Recommendations
2. Market Overview
   1. Market Scope and Definition
   2. Market Dynamics
      1. Drivers
      2. Restraints
      3. Opportunity
      4. Key Trends
   3. Macro-Economic Factors
      1. Global Sectorial Outlook
      2. Global GDP Growth Outlook
   4. COVID-19 Impact Analysis
   5. Forecast Factors - Relevance and Impact
3. Value Added Insights
   1. Treatment Adoption Analysis
   2. Regulatory Landscape
   3. Value Chain Analysis
   4. Key Deals and Mergers
   5. Pipeline Analysis
   6. PESTLE Analysis
   7. Porter’s Five Force Analysis
4. Global Lysosomal Storage Disease Therapeutics Market Outlook:
   1. Key Highlights
      1. Market Size (US$ Bn) and Y-o-Y Growth
      2. Absolute $ Opportunity
   2. Market Size (US$ Bn) Analysis and Forecast
      1. Historical Market Size (US$ Bn) Analysis, 2019-2024
      2. Market Size (US$ Bn) Analysis and Forecast, 2025-2032
   3. Global Lysosomal Storage Disease Therapeutics Market Outlook: Treatment
      1. Introduction / Key Findings
      2. Historical Market Size (US$ Bn) Analysis, By Treatment, 2019-2024
      3. Market Size (US$ Bn) Analysis and Forecast, By Treatment, 2025-2032
         1. Enzyme Replacement Therapy (ERT)
         2. Hematopoietic Stem Cell Transplant
         3. Small Molecule Therapy
         4. Others
      4. Market Attractiveness Analysis: Treatment
   4. Global Lysosomal Storage Disease Therapeutics Market Outlook: Indication
      1. Introduction / Key Findings
      2. Historical Market Size (US$ Bn) Analysis, By Indication, 2019-2024
      3. Market Size (US$ Bn) Analysis and Forecast, By Indication, 2025-2032
         1. Fabry Disease
         2. Gaucher Disease
         3. Mucopolysaccharidosis
         4. Pompe Disease
         5. Krabbe Disease
         6. Others
      4. Market Attractiveness Analysis: Indication
   5. Global Lysosomal Storage Disease Therapeutics Market Outlook: End User
      1. Introduction / Key Findings
      2. Historical Market Size (US$ Bn) Analysis, By End User, 2019-2024
      3. Market Size (US$ Bn) Analysis and Forecast, By End User, 2025-2032
         1. Hospitals
         2. Biopharma Companies
         3. Specialty Clinics
         4. Academic and Research Institutes
         5. Others
      4. Market Attractiveness Analysis: End User
5. Global Lysosomal Storage Disease Therapeutics Market Outlook: Region
   1. Key Highlights
   2. Historical Market Size (US$ Bn) Analysis, By Region, 2019-2024
   3. Market Size (US$ Bn) Analysis and Forecast, By Region, 2025-2032
      1. North America
      2. Europe
      3. East Asia
      4. South Asia and Oceania
      5. Latin America
      6. Middle East & Africa
   4. Market Attractiveness Analysis: Region
6. North America Lysosomal Storage Disease Therapeutics Market Outlook:
   1. Key Highlights
   2. Historical Market Size (US$ Bn) Analysis, By Market, 2019-2024
      1. By Country
      2. By Treatment
      3. By Indication
      4. By End User
   3. Market Size (US$ Bn) Analysis and Forecast, By Country, 2025-2032
      1. U.S.
      2. Canada
   4. Market Size (US$ Bn) Analysis and Forecast, By Treatment, 2025-2032
      1. Enzyme Replacement Therapy (ERT)
      2. Hematopoietic Stem Cell Transplant
      3. Small Molecule Therapy
      4. Others
   5. Market Size (US$ Bn) Analysis and Forecast, By Indication, 2025-2032
      1. Fabry Disease
      2. Gaucher Disease
      3. Mucopolysaccharidosis
      4. Pompe Disease
      5. Krabbe Disease
      6. Others
   6. Market Size (US$ Bn) Analysis and Forecast, By End User, 2025-2032
      1. Hospitals
      2. Biopharma Companies
      3. Specialty Clinics
      4. Academic and Research Institutes
      5. Others
   7. Market Attractiveness Analysis
7. Europe Lysosomal Storage Disease Therapeutics Market Outlook:
   1. Key Highlights
   2. Historical Market Size (US$ Bn) Analysis, By Market, 2019-2024
      1. By Country
      2. By Treatment
      3. By Indication
      4. By End User
   3. Market Size (US$ Bn) Analysis and Forecast, By Country, 2025-2032
      1. Germany
      2. France
      3. U.K.
      4. Italy
      5. Spain
      6. Russia
      7. Türkiye
      8. Rest of Europe
   4. Market Size (US$ Bn) Analysis and Forecast, By Treatment, 2025-2032
      1. Enzyme Replacement Therapy (ERT)
      2. Hematopoietic Stem Cell Transplant
      3. Small Molecule Therapy
      4. Others
   5. Market Size (US$ Bn) Analysis and Forecast, By Indication, 2025-2032
      1. Fabry Disease
      2. Gaucher Disease
      3. Mucopolysaccharidosis
      4. Pompe Disease
      5. Krabbe Disease
      6. Others
   6. Market Size (US$ Bn) Analysis and Forecast, By End User, 2025-2032
      1. Hospitals
      2. Biopharma Companies
      3. Specialty Clinics
      4. Academic and Research Institutes
      5. Others
   7. Market Attractiveness Analysis
8. East Asia Lysosomal Storage Disease Therapeutics Market Outlook:
   1. Key Highlights
   2. Historical Market Size (US$ Bn) Analysis, By Market, 2019-2024
      1. By Country
      2. By Treatment
      3. By Indication
      4. By End User
   3. Market Size (US$ Bn) Analysis and Forecast, By Country, 2025-2032
      1. China
      2. Japan
      3. South Korea
   4. Market Size (US$ Bn) Analysis and Forecast, By Treatment, 2025-2032
      1. Enzyme Replacement Therapy (ERT)
      2. Hematopoietic Stem Cell Transplant
      3. Small Molecule Therapy
      4. Others
   5. Market Size (US$ Bn) Analysis and Forecast, By Indication, 2025-2032
      1. Fabry Disease
      2. Gaucher Disease
      3. Mucopolysaccharidosis
      4. Pompe Disease
      5. Krabbe Disease
      6. Others
   6. Market Size (US$ Bn) Analysis and Forecast, By End User, 2025-2032
      1. Hospitals
      2. Biopharma Companies
      3. Specialty Clinics
      4. Academic and Research Institutes
      5. Others
   7. Market Attractiveness Analysis
9. South Asia & Oceania Lysosomal Storage Disease Therapeutics Market Outlook:
   1. Key Highlights
   2. Historical Market Size (US$ Bn) Analysis, By Market, 2019-2024
      1. By Country
      2. By Treatment
      3. By Indication
      4. By End User
   3. Market Size (US$ Bn) Analysis and Forecast, By Country, 2025-2032
      1. India
      2. Southeast Asia
      3. ANZ
      4. Rest of South Asia & Oceania
   4. Market Size (US$ Bn) Analysis and Forecast, By Treatment, 2025-2032
      1. Enzyme Replacement Therapy (ERT)
      2. Hematopoietic Stem Cell Transplant
      3. Small Molecule Therapy
      4. Others
   5. Market Size (US$ Bn) Analysis and Forecast, By Indication, 2025-2032
      1. Fabry Disease
      2. Gaucher Disease
      3. Mucopolysaccharidosis
      4. Pompe Disease
      5. Krabbe Disease
      6. Others
   6. Market Size (US$ Bn) Analysis and Forecast, By End User, 2025-2032
      1. Hospitals
      2. Biopharma Companies
      3. Specialty Clinics
      4. Academic and Research Institutes
      5. Others
   7. Market Attractiveness Analysis
10. Latin America Lysosomal Storage Disease Therapeutics Market Outlook:
    1. Key Highlights
    2. Historical Market Size (US$ Bn) Analysis, By Market, 2019-2024
       1. By Country
       2. By Treatment
       3. By Indication
       4. By End User
    3. Market Size (US$ Bn) Analysis and Forecast, By Country, 2025-2032
       1. Brazil
       2. Mexico
       3. Rest of Latin America
    4. Market Size (US$ Bn) Analysis and Forecast, By Treatment, 2025-2032
       1. Enzyme Replacement Therapy (ERT)
       2. Hematopoietic Stem Cell Transplant
       3. Small Molecule Therapy
       4. Others
    5. Market Size (US$ Bn) Analysis and Forecast, By Indication, 2025-2032
       1. Fabry Disease
       2. Gaucher Disease
       3. Mucopolysaccharidosis
       4. Pompe Disease
       5. Krabbe Disease
       6. Others
    6. Market Size (US$ Bn) Analysis and Forecast, By End User, 2025-2032
       1. Hospitals
       2. Biopharma Companies
       3. Specialty Clinics
       4. Academic and Research Institutes
       5. Others
    7. Market Attractiveness Analysis
11. Middle East & Africa Lysosomal Storage Disease Therapeutics Market Outlook:
    1. Key Highlights
    2. Historical Market Size (US$ Bn) Analysis, By Market, 2019-2024
       1. By Country
       2. By Treatment
       3. By Indication
       4. By End User
    3. Market Size (US$ Bn) Analysis and Forecast, By Country, 2025-2032
       1. GCC Countries
       2. Egypt
       3. South Africa
       4. Northern Africa
       5. Rest of Middle East & Africa
    4. Market Size (US$ Bn) Analysis and Forecast, By Treatment, 2025-2032
       1. Enzyme Replacement Therapy (ERT)
       2. Hematopoietic Stem Cell Transplant
       3. Small Molecule Therapy
       4. Others
    5. Market Size (US$ Bn) Analysis and Forecast, By Indication, 2025-2032
       1. Fabry Disease
       2. Gaucher Disease
       3. Mucopolysaccharidosis
       4. Pompe Disease
       5. Krabbe Disease
       6. Others
    6. Market Size (US$ Bn) Analysis and Forecast, By End User, 2025-2032
       1. Hospitals
       2. Biopharma Companies
       3. Specialty Clinics
       4. Academic and Research Institutes
       5. Others
    7. Market Attractiveness Analysis
12. Competition Landscape
    1. Market Share Analysis, 2024
    2. Market Structure
       1. Competition Intensity Mapping By Market
       2. Competition Dashboard
    3. Company Profiles (Details - Overview, Financials, Strategy, Recent Developments)
       1. Polaryx Therapeutics
          1. Overview
          2. Segments and Treatment Types
          3. Key Financials
          4. Market Developments
          5. Market Strategy
       2. M6P therapeutics
       3. Sanofi
       4. Denali Therapeutics
       5. ZYTHERA
       6. BioMarin
       7. Sangamo Therapeutics, Inc
       8. JCR Pharmaceuticals Co., Ltd.
       9. Takeda Pharmaceutical Company Limited
       10. Azafaros B.V.
       11. CIBER & JUMISC
       12. Gain Therapeutics, Inc.
       13. Chiesi Group
       14. Amicus Therapeutics
       15. CANbridge Life Sciences Ltd.
       16. Beijing GeneCradle Technology Co., Ltd.
       17. GC Biopharma
13. Appendix
    1. Research Methodology
    2. Research Assumptions
    3. Acronyms and Abbreviations